Tags » Rare Disease

Sleep > Writing a blog post at almost midnight

What in the world am I doing up this late?

Oh, yeah.  My anxiety is flaring.  Big time.

But I had a good day today.  It started out well.  702 more words

Rare Disease

Europe’s December 2014 Products Recommended For Orphan Drug Designation

The European Medicines Agency (EMA) Committee for Orphan Medicinal Products (COMP) held a meeting December 9 – 11, 2014.

At this meeting, there are 22 positive opinions recommending the following medicines for designation as orphan medicinal products. 417 more words

Orphan Drug Development

Celebrating a memorable 2014 for Uplifting Athletes

Uplifting Athletes has plenty to celebrate in as we near the end of our seventh year as a national non-profit.

The continued support of our expanding coast-to-coast network of student-athlete led chapters is the main reason for our success. 397 more words


My "Normal"

Normal. It is a six letter word. It is a word that I think is used far too often, and can have such different meanings to a wide variety of people. 474 more words

Bumpy Bones

Hunter Syndrome: Shire Collaboration And FDA Acceptance Of ArmaGen’s IND

ArmaGen, a Calabasas, California-based clinical stage biotechnology company  developing therapies for severe neurological disorders, announces December 11th, that the FDA’s Investigational New Drug (IND) application for the company’s lead product candidate, AGT-182 for Hunter Syndrome (Muchopolysaccharidosis II or MPS II), is accepted and is now active. 301 more words

Orphan Drug Development