Blogs about: Rare Diseases
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why we do what we do
on diagnosis “When newly diagnosed the impact on the person/ family is like a bomb going off- everyone is stunned, the air is cloudy and you can’t see the way forward. You feel stuck in time, stranded… more →
me, mine and other bits
New search engine finds rare diagnoses
wrote 3 hours ago: (Technical University of Denmark 21 May 2013) Doctors are trained to think “common disease … more →
Rare Diseases And Orphan Drugs: Gene Therapy Business Developments #2
wrote 23 hours ago: Gene therapy for rare genetic diseases is hot news in biotechnology. Biotechnology companies that de … more →
Costs and profits around orphan drugs
wrote 1 day ago: At the Bloomberg site, an article released on the 23rd January 2012, was written about BioMarin´s ac … more →
Rare Diseases And Orphan Drugs: Gene Therapy Business Developments #1
wrote 2 days ago: Gene therapy for rare genetic diseases is hot news in biotechnology. Biotechnology companies that de … more →
A special type of lodge
wrote 4 days ago: Nearly every big company has some sort of a corporate social responsibility program. Motives can som … more →
Orphan Drug Biotechs Do It Best
wrote 4 days ago: Source: The Motley Fool By Terry Chrisomalis There are many biotech stocks to choose from that have … more →
Virtual zeal: rare disease caregivers carry a powerful voice in social media
wrote 4 days ago: Source: PharmaPhorum This article highlights how rare disease patients and caregivers can harness … more →
Orphan Drugs And Rare Diseases: Global News (05.17.13)
wrote 4 days ago: Recent orphan drug and rare disease global developments are in the news. Here is a list and descript … more →
"This girl is on fire."
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wrote 5 days ago: I’m new at this blog thing but I feel the need to share my story in an attempt to bring awaren … more →
The Deadline is Friday for Helping Grow the Rare Disease Congressional Caucus
wrote 5 days ago: Friday, May 17 at 8PM eastern is the deadline for this. We want to have Caucus Members from all 50 S … more →
Orphan Drugs And Rare Diseases: Partnerships And Collaborations
wrote 5 days ago: The following discusses new partnerships and collaborations in the area of orphan drugs and rare dis … more →
The Advocate
wrote 6 days ago: The American Society of Gene & Cell Therapy’s annual conference kicked off early this morn … more →
Orphan Drugs: FDA PDUFA Dates June – October 2013 (05.15.13)
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wrote 1 week ago: Investors and traders will be watching several orphan drug FDA PDUFA dates for June through October … more →
Spells and Potions
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wrote 1 week ago: I will love the light for it shows me the way, yet I will endure the darkness because it shows me th … more →
Hyperthyroidism due to thyroid stimulating hormone secretion after surgery for Cushing's syndrome: A novel cause of the syndrome of inappropriate secretion of thyroid stimulating hormone
wrote 1 week ago: Overview of the thyroid system (See Wikipedia:Thyroid). To discuss image, please see Talk:Human body … more →
2013 Orphan Drug And Rare Disease Meeting Calendar (05.14.13)
wrote 1 week ago: 2013 Orphan Drug and Rare Disease Meeting Calendar as of 05.14.13 : - World Orphan Drug Congress Asi … more →
Gleevec: New Book On The Journey Of Discovery
wrote 1 week ago: The book. “The Philadelphia Chromosome: A Mutant Gene and the Quest to Cure Cancer at the Genetic Le … more →
Secrets of a Scaredy Cat: How to put your fear into perspective.
wrote 1 week ago: “There are two kinds of fears: rational and irrational- or in simpler terms, fears that make sense a … more →
Help Grow the Rare Disease Congressional Caucus
wrote 1 week ago: The Rare Disease Congressional Caucus will help bring public and Congressional awareness to the uniq … more →
